Thomas Gaj

Biochemistry, Genetics and Molecular Biology

Pilot corpus only

This score is computed over theSindex pilot corpus and does not cover the full scientific literature. Scores are relative to papers we have ingested — papers, authors, and institutions outside the pilot are not represented. Methodology.

Top 100%percentile

0Author DataRank

Indexed papers

0in pilot corpus

datarank_citation_only_1hop_v6· scope data_onlyMethodology

Papers

Driven by 10 papers. Top paper: “Mitigating a TDP-43 proteinopathy by targeting ataxin-2 using RNA-targeting CRISPR effector proteins”.

Mitigating a TDP-43 proteinopathy by targeting ataxin-2 using RNA-targeting CRISPR effector proteins

Nature Communications(2023)10.1038/s41467-023-42147-z

N/A

0.985DataRank · unranked

38 citations

Hayden J. Moore, Tyler Smith, Jackson E. Powell, Najah S. Ahsan, Sijia Zhang +2 more

SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skipping

Nature Communications(2024)10.1038/s41467-024-54529-y

N/A

0.339DataRank · unranked

5 citations

Shraddha Shirguppe, Jackson Winter, Gianna Elias, Devyani Swami, Ananthan Nambiar +10 more

A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTD

bioRxiv (Cold Spring Harbor Laboratory)(2023)10.1101/2023.12.12.571328

N/A

0DataRank · unranked

4 citations

Colin K.W. Lim, William M. Terpstra, M. Alejandra Zeballos C., Sijia Zhang, Jackson E. Powell +2 more

Mitigating a TDP-43 proteinopathy by targeting ataxin-2 using RNA-targeting CRISPR effector proteins

bioRxiv (Cold Spring Harbor Laboratory)(2023)10.1101/2023.04.07.536072

N/A

0DataRank · unranked

2 citations

Hayden J. Moore, Tyler Smith, Jackson E. Powell, Najah S. Ahsan, Sijia Zhang +2 more

In vivo CRISPR base editing for treatment of Huntington’s disease

bioRxiv (Cold Spring Harbor Laboratory)(2024)10.1101/2024.07.05.602282

N/A

0DataRank · unranked

4 citations

Michael Gapinske, Devyani Swami, Nicholas Gosstola, Pankaj Acharya, Angelo Miskalis +12 more

SPLICER: A Highly Efficient Base Editing Toolbox That Enables In Vivo Therapeutic Exon Skipping

bioRxiv (Cold Spring Harbor Laboratory)(2024)10.1101/2024.04.01.587650

N/A

0DataRank · unranked

2 citations

Shraddha Shirguppe, Jackson Winter, Gianna Elias, Devyani Swami, Ananthan Nambiar +10 more

A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTD

Nature Communications(2025)10.1038/s41467-024-55548-5

N/A

0DataRank · unranked

16 citations

Colin K.W. Lim, Mayuri Singh, Sijia Zhang, Najah S. Ahsan, William M. Terpstra +7 more

Next-Generation CRISPR Technologies and Their Applications in Gene and Cell Therapy

Trends in biotechnology(2020)10.1016/j.tibtech.2020.10.010

N/A

0DataRank · unranked

95 citations

Thomas Gaj, M. Alejandra Zeballos C.

Treatment of Huntington’s disease with a pan-HTT-targeting CRISPR nuclease

bioRxiv (Cold Spring Harbor Laboratory)(2025)10.64898/2025.12.20.695720

N/A

0DataRank · unranked

0 citations

Daniela Del Bosque Siller, A. Xiong, Anna X.A. Wang, Tristan X. McCallister, Sreya Mummadi +11 more

CRISPR base editing of cis -regulatory elements enables target gene perturbations

bioRxiv (Cold Spring Harbor Laboratory)(2022)10.1101/2022.05.26.493649

N/A

0DataRank · unranked

0 citations

Tristan X. McCallister, Christian Saporito-Magriñá, Garrett D. McPheron, Ramya Krishnan, M. Alejandra Zeballos C. +5 more