Steven J. Gray

Also affiliated with The University of Texas Southwestern Medical Center

Biochemistry, Genetics and Molecular BiologyMedicine

Pilot corpus only

This score is computed over theSindex pilot corpus and does not cover the full scientific literature. Scores are relative to papers we have ingested — papers, authors, and institutions outside the pilot are not represented. Methodology.

Top 100%percentile

0Author DataRank

Indexed papers

0in pilot corpus

datarank_citation_only_1hop_v6· scope data_onlyMethodology

Papers

Driven by 23 papers. Top paper: “Intrathecal Gene Therapy for Giant Axonal Neuropathy”.

Intrathecal Gene Therapy for Giant Axonal Neuropathy

New England Journal of Medicine(2024)10.1056/nejmoa2307952

N/A

1.4DataRank · unranked

59 citations

Joshua J. Todd, Dimah Saade, Gina Norato, Minal Jain, Tanya Lehky +24 more

Current Clinical Applications of In Vivo Gene Therapy with AAVs

Molecular Therapy(2020)10.1016/j.ymthe.2020.12.007

N/A

0.993DataRank · unranked

748 citations

Samiah Al-Zaidy, Louise R. Rodino‐Klapac, Kimberly Goodspeed, Steven J. Gray, Christine N. Kay +7 more

Intrathecal AAV9/AP4M1 gene therapy for hereditary spastic paraplegia 50 shows safety and efficacy in preclinical studies

Journal of Clinical Investigation(2023)10.1172/jci164575

N/A

0.571DataRank · unranked

44 citations

Thomas Dong, Yuhui Hu, Raffaella De Pace, Rafael Mattera, Kathrin Eberhardt +7 more

Focused ultrasound widely broadens AAV-delivered Cas9 distribution and activity

Gene Therapy(2025)10.1038/s41434-025-00517-w

N/A

0.292DataRank · unranked

6 citations

Sahba Kasiri, Ibrahim Youssef, Mayank Verma, Rajiv Chopra, Daniel Villarreal +9 more

SMRT Sequencing Enables High-Throughput Identification of Novel AAVs from Capsid Shuffling and Directed Evolution

Genes(2023)10.3390/genes14081660

N/A

0.281DataRank · unranked

4 citations

Irvin T. Garza, Xin Chen, Thomas Dong, Yuhui Hu, Mohammed Kanchwala +7 more

Optimization of scAAVIL-1ra In Vitro and In Vivo to Deliver High Levels of Therapeutic Protein for Treatment of Osteoarthritis

UNC Libraries(2020)10.17615/g59r-mw33

N/A

0DataRank · unranked

0 citations

R. Jude Samulski, Joshua C. Grieger, Jennifer N. Phillips, Laurie R. Goodrich, C Wayne McIlwraith +2 more

Intrathecal administration of AAV/GALC vectors in 10-11-day-old twitcher mice improves survival and is enhanced by bone marrow transplant: Intrathecal AAV Combined With BMT To Treat Krabbe Disease

UNC Libraries(2020)10.17615/k41h-ea43

N/A

0DataRank · unranked

0 citations

Clifford Heindel, Ernesto R. Bongarzone, Michael S. Marshall, Steven J. Gray, Subha Karumuthil‐Melethil +1 more

Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome

UNC Libraries(2020)10.17615/41zk-qg33

N/A

0DataRank · unranked

0 citations

Ralph D. Hector, Mark E.S. Bailey, Kamal K.E. Gadalla, Noha Bahey, Stuart Cobb +3 more

Autonomic nervous system involvement in the giant axonal neuropathy (GAN) KO mouse: implications for human disease

UNC Libraries(2020)10.17615/5zdv-0g21

N/A

0DataRank · unranked

0 citations

Yongbaek Kim, Steven J. Gray, Rachel M. Bailey, Diane Armao, Thomas W. Bouldin

Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

UNC Libraries(2020)10.17615/k4e8-xw30

N/A

0DataRank · unranked

0 citations

L. Govindasamy, Juan Li, Chengwen Li, Dawn E. Bowles, Xiao Xiao +10 more

Engineered microRNA-based regulatory element permits safe high-dose miniMECP2gene therapy in Rett mice

Brain(2021)10.1093/brain/awab182

N/A

0DataRank · unranked

73 citations

Emily Boyle, Christopher J. Lyons, Steven J. Gray, Sarah E. Sinnett

Giant axonal neuropathy: cross-sectional analysis of a large natural history cohort

Brain(2021)10.1093/brain/awab179

N/A

0DataRank · unranked

38 citations

Gina Norato, Dimah Saade, Eduardo Paredes, Victoria Biancavilla, Sandra Donkervoort +14 more

AAV9-mediated FIG4 delivery prolongs life span in Charcot-Marie-Tooth disease type 4J mouse model

Journal of Clinical Investigation(2021)10.1172/jci137159

N/A

0DataRank · unranked

33 citations

Rachel M. Bailey, Crystal Davis, Tara Murphy, Jenn Cook, Randy Walls +7 more

Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disorders

Molecular Therapy(2022)10.1016/j.ymthe.2022.05.014

N/A

0DataRank · unranked

26 citations

Guangping Gao, Elizabeth Berry‐Kravis, Allison M. Bradbury, Carsten G. Bönnemann, Joseph D. Buxbaum +12 more

Preclinical use of a clinically-relevant scAAV9/SUMF1 vector for the treatment of multiple sulfatase deficiency

Communications Medicine(2025)10.1038/s43856-025-00734-9

N/A

0DataRank · unranked

2 citations

Rachel M. Bailey, Somdatta Ray, Lauren Bailey, Saurabh Tata, Tara Murphy +5 more

Plasmonic Nanopore Sensing to Probe the DNA Loading Status of Adeno-Associated Viruses

Chemosensors(2025)10.3390/chemosensors13120418

N/A

0DataRank · unranked

2 citations

Steven J. Gray, Min Jun Kim, George Alexandrakis, Scott Renkes

First-in-human high dose AAV9 intrathecal gene therapy for paediatric CLN7 disease: a phase 1, open-label, single ascending dose, non-randomised clinical trial

EBioMedicine(2025)10.1016/j.ebiom.2025.106044

N/A

0DataRank · unranked

1 citations

Berge A. Minassian, Souad Messahel, Veronica Bordes Edgar, Andrea Lowden, Hamza Dahshi +10 more

Age-sensitive response of systemic AAV-mediated gene therapy in a newly characterized feline model of mucolipidosis II

Molecular Therapy(2025)10.1016/j.ymthe.2025.04.030

N/A

0DataRank · unranked

1 citations

Jessica Bagel, Charles Shyng, Patricia M. O’Donnell, Keiko Miyadera, Jennifer Srnak +10 more

T2 Hyperintensities in Gracile Tracts of Cervical Spinal Cord in Giant Axonal Neuropathy ( GAN )

Muscle & Nerve(2025)10.1002/mus.70004

N/A

0DataRank · unranked

0 citations

Thomas W. Bouldin, Diana Bharucha‐Goebel, Terry Hartman, Steven J. Gray, Rachel M. Bailey +7 more

Comparison of high-dose intracisterna magna and lumbar puncture intrathecal delivery of AAV9 in mice to treat neuropathies

Brain Research(2020)10.1016/j.brainres.2020.146832

N/A

0DataRank · unranked

85 citations

Alejandra Rozenberg, Steven J. Gray, Rachel M. Bailey

Krabbe disease successfully treated via monotherapy of intrathecal gene therapy

Journal of Clinical Investigation(2020)10.1172/jci133953

N/A

0DataRank · unranked

70 citations

Jessica Bagel, Duc Nguyen, Erik Lykken, Jill Pesayco Salvador, Xuntian Jiang +14 more

Intellectual and Developmental Disabilities Research Centers: A Multidisciplinary Approach to Understand the Pathogenesis of Methyl-CpG Binding Protein 2-related Disorders

Neuroscience(2020)10.1016/j.neuroscience.2020.04.037

N/A

0DataRank · unranked

20 citations

Annarita Patrizi, Jocelyn J. LeBlanc, Lee‐Way Jin, Izumi Maezawa, Sarah E. Sinnett +13 more

Progress in gene therapy for neurological disorders

UNC Libraries(2020)10.17615/r0mf-tr10

N/A

0DataRank · unranked

0 citations

Nicholas M. Boulis, Thomas J. Wilson, William F. Goins, Jean Bennett, John H. Wolfe +7 more