Heather Gray‐Edwards

Also affiliated with University of Massachusetts Chan Medical School

Biochemistry, Genetics and Molecular BiologyMedicine

Pilot corpus only

This score is computed over theSindex pilot corpus and does not cover the full scientific literature. Scores are relative to papers we have ingested — papers, authors, and institutions outside the pilot are not represented. Methodology.

Top 100%percentile

0Author DataRank

Indexed papers

0in pilot corpus

datarank_citation_only_1hop_v6· scope data_onlyMethodology

Papers

Driven by 25 papers. Top paper: “Therapeutic benefit after intracranial gene therapy delivered during the symptomatic stage in a feline model of Sandhoff disease”.

Therapeutic benefit after intracranial gene therapy delivered during the symptomatic stage in a feline model of Sandhoff disease

Gene Therapy(2020)10.1038/s41434-020-00190-1

N/A

0.590DataRank · unranked

16 citations

Aime K. Johnson, Heather Gray‐Edwards, Ashley N. Randle, Allison M. Bradbury, Nancy E. Morrison +6 more

Treatment of a severe vascular disease using a bespoke CRISPR–Cas9 base editor in mice

Nature Biomedical Engineering(2025)10.1038/s41551-025-01499-1

N/A

0.342DataRank · unranked

8 citations

Sabyasachi Das, Vijai Krishnan, Leillani L. Ha, Lauren R. Fox, Hannah E. Stutzman +28 more

AAV9 Gene Therapy in GM1 Gangliosidosis Type II: A Phase 1/2 Trial

medRxiv(2025)10.1101/2025.07.28.25332074

N/A

0.212DataRank · unranked

3 citations

Precilla D’Souza, Jean M. Johnston, Maria T. Acosta, Cristan Farmer, Eva H. Baker +27 more

PEA15 loss of function and defective cerebral development in the domestic cat

PLoS Genetics(2020)10.1371/journal.pgen.1008671

N/A

0DataRank · unranked

7 citations

J. Nicholas Cochran, Christopher B. Kaelin, Kenneth Day, Heather Gray‐Edwards, Rie Watanabe +8 more

Abnormal epiphyseal development in a feline model of Sandhoff disease

Journal of Orthopaedic Research®(2020)10.1002/jor.24803

N/A

0DataRank · unranked

6 citations

Patricia B. Prevatt, Elizabeth R. Nussbaum, Ashley N. Randle, Aime K. Johnson, Judith A. Hudson +5 more

Suppression of mutant C9orf72 expression by a potent mixed backbone antisense oligonucleotide

Nature Medicine(2021)10.1038/s41591-021-01557-6

N/A

0DataRank · unranked

175 citations

Michael P. Moazami, Huiya Yang, Diane McKenna‐Yasek, Catherine Douthwright, Courtney Pinto +16 more

A comprehensive study of a 29-capsid AAV library in a non-human primate central nervous system

Molecular Therapy(2021)10.1016/j.ymthe.2021.07.010

N/A

0DataRank · unranked

62 citations

Liudmyla Kondratova, Ronald J. Mandel, Kirsten E. Coleman, Michael A. Savage, Heather Gray‐Edwards +7 more

Comparative route of administration studies using therapeutic siRNAs show widespread gene modulation in Dorset sheep

JCI Insight(2021)10.1172/jci.insight.152203

N/A

0DataRank · unranked

29 citations

Bruno M.D.C. Godinho, Julia F. Alterman, Andrew H. Coles, Matthew Hassler, Dimas Echeverria +13 more

Real-time MR tracking of AAV gene therapy with βgal-responsive MR probe in a murine model of GM1-gangliosidosis

Molecular Therapy — Methods & Clinical Development(2021)10.1016/j.omtm.2021.08.003

N/A

0DataRank · unranked

17 citations

Ana Rita Batista, Sarah Kamper, Michael A. Caldwell, Laura M. Lilley, Hao Li +12 more

Natural history of Tay-Sachs disease in sheep

Molecular Genetics and Metabolism(2021)10.1016/j.ymgme.2021.08.009

N/A

0DataRank · unranked

12 citations

Toloo Taghian, Jillian Gallagher, Jennifer W. Koehler, Amanda R. Taylor, Ashley N. Randle +16 more

Quantifying and Mitigating Motor Phenotypes Induced by Antisense Oligonucleotides in the Central Nervous System

bioRxiv (Cold Spring Harbor Laboratory)(2021)10.1101/2021.02.14.431096

N/A

0DataRank · unranked

17 citations

Julia M Rembetsy-Brown, Feng Wang, Pranathi M. Krishnamurthy, Alexandra Weiss, Miklós Marosföi +7 more

Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disorders

Molecular Therapy(2022)10.1016/j.ymthe.2022.05.014

N/A

0DataRank · unranked

26 citations

Guangping Gao, Elizabeth Berry‐Kravis, Allison M. Bradbury, Carsten G. Bönnemann, Joseph D. Buxbaum +12 more

A pentasaccharide for monitoring pharmacodynamic response to gene therapy in GM1 gangliosidosis

EBioMedicine(2023)10.1016/j.ebiom.2023.104627

N/A

0DataRank · unranked

21 citations

Rohini Sidhu, Mingxing Qian, Sonali Mishra, Elena‐Raluca Nicoli, Precilla D’Souza +12 more

Precision medicine using whole genome sequencing in a cat identifies a novel COL5A1 variant for classical Ehlers-Danlos syndrome

Journal of Veterinary Internal Medicine(2023)10.1111/jvim.16805

N/A

0DataRank · unranked

7 citations

Heather Gray‐Edwards, Lyndon M. Coghill, Leslie A. Lyons, Abigail McElroy

Life‐Limiting Peripheral Organ Dysfunction in Feline Sandhoff Disease Emerges after Effective CNS Gene Therapy

Annals of Neurology(2023)10.1002/ana.26756

N/A

0DataRank · unranked

6 citations

Victoria J. McCurdy, Heather Gray‐Edwards, Anne S. Maguire, J. Nicholas Cochran, Amanda L. Gross +14 more

Awake intracerebroventricular delivery and safety assessment of oligonucleotides in a large animal model

Molecular Therapy — Methods & Clinical Development(2023)10.1016/j.omtm.2023.101122

N/A

0DataRank · unranked

3 citations

Rachel Prestigiacomo, Toloo Taghian, Rachael Miller, R King, Matthew J. Gounis +13 more

Quantifying and mitigating motor phenotypes induced by antisense oligonucleotides in the central nervous system

Molecular Therapy(2024)10.1016/j.ymthe.2024.10.024

N/A

0DataRank · unranked

26 citations

Julia M Rembetsy-Brown, Samantha L. Sarli, Holly R McEachern, Feng Wang, Masahiro Ohara +12 more

Quantitative reliability assessment of brain MRI volumetric measurements in type II GM1 gangliosidosis patients

Frontiers in Neuroimaging(2024)10.3389/fnimg.2024.1410848

N/A

0DataRank · unranked

6 citations

Josephine Kolstad, Jean M. Johnston, Precilla D’Souza, Anna Luisa Kühn, Zeynep Vardar +10 more

Natural history progression of MRI brain volumetrics in type II late-infantile and juvenile GM1 gangliosidosis patients

Molecular Genetics and Metabolism(2025)10.1016/j.ymgme.2025.109025

N/A

0DataRank · unranked

7 citations

Christopher Zoppo, Jean M. Johnston, Precilla D’Souza, Anna Luisa Kühn, Zeynep Vardar +14 more

Corrigendum to “Natural history progression of MRI brain volumetrics in type II late-infantile and juvenile GM1 gangliosidosis patients” [Molecular Genetics and Metabolism 2025 Mar;144(3):109025].

Molecular Genetics and Metabolism(2025)10.1016/j.ymgme.2025.109109

N/A

0DataRank · unranked

0 citations

Christopher Zoppo, Jean M. Johnston, Precilla D’Souza, Anna Luisa Kühn, Zeynep Vardar +14 more

Secondary accumulation of lyso-platelet activating factors in lysosomal storage diseases

Molecular Genetics and Metabolism(2025)10.1016/j.ymgme.2025.109180

N/A

0DataRank · unranked

0 citations

Sonali Mishra, Heather Gray‐Edwards, Douglas R. Martin, Angel Gaudioso, María Dolores Ledesma +6 more

Canine Models of Inherited Musculoskeletal and Neurodegenerative Diseases

Frontiers in Veterinary Science(2020)10.3389/fvets.2020.00080

N/A

0DataRank · unranked

26 citations

Matthew Miller, Allison M. Bradbury, Emily D. Million, Dongsheng Duan, Toloo Taghian +5 more

Intracerebroventricular SPAST-AAV9 gene therapy prevents manifestation of symptoms in a mouse model of SPG4 hereditary spastic paraplegia

Molecular Therapy(2025)10.1016/j.ymthe.2025.11.029

N/A

0DataRank · unranked

0 citations

Shrobona Guha, Liang Qiang, Heather Gray‐Edwards, Miguel Sena‐Esteves, Peter W. Baas +1 more

Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice

Molecular Therapy(2020)10.1016/j.ymthe.2020.06.021

N/A

0DataRank · unranked

36 citations

Chelsea Joy Webber, Diane Golebiowski, C Izzo, Erin Horn, Toloo Taghian +8 more

Large Animal Models of Huntington’s Disease: What We Have Learned and Where We Need to Go Next

Journal of Huntington s Disease(2020)10.3233/jhd-200425

N/A

0DataRank · unranked

36 citations

Zdeňka Ellederová, Neil Aronin, Deborah Fernau, Jill Gallagher, Amanda R. Taylor +5 more