Miguel Sena‐Esteves

University of Massachusetts Chan Medical School

Biochemistry, Genetics and Molecular BiologyMedicine

Pilot corpus only

This score is computed over theSindex pilot corpus and does not cover the full scientific literature. Scores are relative to papers we have ingested — papers, authors, and institutions outside the pilot are not represented. Methodology.

Top 100%percentile

0Author DataRank

Indexed papers

0in pilot corpus

datarank_citation_only_1hop_v6· scope data_onlyMethodology

Papers

Driven by 16 papers. Top paper: “Therapeutic benefit after intracranial gene therapy delivered during the symptomatic stage in a feline model of Sandhoff disease”.

Therapeutic benefit after intracranial gene therapy delivered during the symptomatic stage in a feline model of Sandhoff disease

Gene Therapy(2020)10.1038/s41434-020-00190-1

N/A

0.590DataRank · unranked

16 citations

Aime K. Johnson, Heather Gray‐Edwards, Ashley N. Randle, Allison M. Bradbury, Nancy E. Morrison +6 more

Focused Ultrasound-Mediated Disruption of the Blood–Brain Barrier for AAV9 Delivery in a Mouse Model of Huntington’s Disease

Pharmaceutics(2024)10.3390/pharmaceutics16060710

N/A

0.396DataRank · unranked

13 citations

Yongzhi Zhang, Lilyan Garrett, Alvin Yao, Kai Shing, Ana Rita Batista +5 more

AAV9 Gene Therapy in GM1 Gangliosidosis Type II: A Phase 1/2 Trial

medRxiv(2025)10.1101/2025.07.28.25332074

N/A

0.212DataRank · unranked

3 citations

Precilla D’Souza, Jean M. Johnston, Maria T. Acosta, Cristan Farmer, Eva H. Baker +27 more

EZH2 inhibition reactivates epigenetically silenced FMR1 and normalizes molecular and electrophysiological abnormalities in fragile X syndrome neurons

Frontiers in Neuroscience(2024)10.3389/fnins.2024.1348478

N/A

0.104DataRank · unranked

1 citations

Sara K. Evans, Pranathi M. Krishnamurthy, Feng Wang, Paola Rodrı́guez, Shahid Banday +5 more

Gene Therapy: Charting a Future Course—Summary of a National Institutes of Health Workshop, April 12, 2013

UNC Libraries(2020)10.17615/bazj-3394

N/A

0DataRank · unranked

0 citations

Howard J. Federoff, Luk H. Vandenberghe, Aravind Asokan, Mehrdad Abedi, Laurie Zoloth +27 more

Real-time MR tracking of AAV gene therapy with βgal-responsive MR probe in a murine model of GM1-gangliosidosis

Molecular Therapy — Methods & Clinical Development(2021)10.1016/j.omtm.2021.08.003

N/A

0DataRank · unranked

17 citations

Ana Rita Batista, Sarah Kamper, Michael A. Caldwell, Laura M. Lilley, Hao Li +12 more

Natural history of Tay-Sachs disease in sheep

Molecular Genetics and Metabolism(2021)10.1016/j.ymgme.2021.08.009

N/A

0DataRank · unranked

12 citations

Toloo Taghian, Jillian Gallagher, Jennifer W. Koehler, Amanda R. Taylor, Ashley N. Randle +16 more

Excessive release of inorganic polyphosphate by ALS/FTD astrocytes causes non-cell-autonomous toxicity to motoneurons

Neuron(2022)10.1016/j.neuron.2022.02.010

N/A

0DataRank · unranked

88 citations

Carolina Cefaliello, Agnieszka Dyrda, Nur Jury, Pablo Martínez, Iván Darío Parrado Díaz +32 more

Life‐Limiting Peripheral Organ Dysfunction in Feline Sandhoff Disease Emerges after Effective CNS Gene Therapy

Annals of Neurology(2023)10.1002/ana.26756

N/A

0DataRank · unranked

6 citations

Victoria J. McCurdy, Heather Gray‐Edwards, Anne S. Maguire, J. Nicholas Cochran, Amanda L. Gross +14 more

Awake intracerebroventricular delivery and safety assessment of oligonucleotides in a large animal model

Molecular Therapy — Methods & Clinical Development(2023)10.1016/j.omtm.2023.101122

N/A

0DataRank · unranked

3 citations

Rachel Prestigiacomo, Toloo Taghian, Rachael Miller, R King, Matthew J. Gounis +13 more

Expression of ALS-PFN1 impairs vesicular degradation in iPSC-derived microglia

bioRxiv (Cold Spring Harbor Laboratory)(2023)10.1101/2023.06.01.541136

N/A

0DataRank · unranked

4 citations

Del Hayden Gadd, Michelle Mosqueda, Jianjun Zhong, Jonathan Jung, Shankaracharya +15 more

Expression of ALS-PFN1 impairs vesicular degradation in iPSC-derived microglia

Nature Communications(2024)10.1038/s41467-024-46695-w

N/A

0DataRank · unranked

23 citations

Jonathan Jung, Del Hayden Gadd, Michelle Mosqueda, Jianjun Zhong, Shankaracharya +19 more

Intracerebroventricular SPAST-AAV9 gene therapy prevents manifestation of symptoms in a mouse model of SPG4 hereditary spastic paraplegia

Molecular Therapy(2025)10.1016/j.ymthe.2025.11.029

N/A

0DataRank · unranked

0 citations

Shrobona Guha, Liang Qiang, Heather Gray‐Edwards, Miguel Sena‐Esteves, Peter W. Baas +1 more

Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice

Molecular Therapy(2020)10.1016/j.ymthe.2020.06.021

N/A

0DataRank · unranked

36 citations

Chelsea Joy Webber, Diane Golebiowski, C Izzo, Erin Horn, Toloo Taghian +8 more

Upregulating β-hexosaminidase activity in rodents prevents α-synuclein lipid associations and protects dopaminergic neurons from α-synuclein-mediated neurotoxicity

Acta Neuropathologica Communications(2020)10.1186/s40478-020-01004-6

N/A

0DataRank · unranked

24 citations

Joanna A. Korecka, Cécile C. Crapart, Mylene Huebecker, Zachary K. Macbain, Sara Ann Rosenthal +6 more

Abnormal epiphyseal development in a feline model of Sandhoff disease

Journal of Orthopaedic Research®(2020)10.1002/jor.24803

N/A

0DataRank · unranked

6 citations

Patricia B. Prevatt, Elizabeth R. Nussbaum, Ashley N. Randle, Aime K. Johnson, Judith A. Hudson +5 more