Screening data from 19 patients with late‐onset Pompe disease for a phase I clinical trial of AAV8 vector‐mediated gene therapy

Screening data from 19 patients with late‐onset Pompe disease for a phase I clinical trial of AAV8 vector‐mediated gene therapy is a research paper published in JIMD Reports (2023). On theSindex it has a DataRank of 0. It has been cited 2 times.