Effect of disease progression on CSF-directed AAV gene therapy in a large brain animal model of lysosomal storage disease is a research paper published in Molecular Therapy — Methods & Clinical Development (2025). On theSindex it has a DataRank of 0.
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National Institutes of Health
Grant: R01-DK063973
National Institutes of Health
Grant: P40-OD010939
National Institutes of Health
Grant: R01-NS110349
National Institutes of Health
Grant: 3R01DK063973-06A2S1
Gene Transfer and NMR Studies in Alpha-Mannosidosis Brain
National Institutes of Health
Grant: 1R01NS110349-01A1
Translational studies on cerebrospinal fluid (CSF)-directed gene therapy for global neurometabolic brain disease
National Institutes of Health
Grant: 5P40OD010939-33
Referral Center-Animal models of human genetic disease
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