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Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease

Molecular Therapy(2020)10.1016/j.ymthe.2020.12.031Source: DataRank Database

Enhanced Efficacy and Increased Long-Term Toxicity of CNS-Directed, AAV-Based Combination Therapy for Krabbe Disease is a research paper published in Molecular Therapy (2020). On theSindex it has a DataRank of 0. It has been cited 50 times.

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0DataRank · unranked

Scored on demand from live citation data

Open Access50 citations

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›Methodology & internals

datarank_citation_only_1hop_v6· scope data_onlyMethodology

Pipeline:MetadataData-paper checkEnrichmentCitation networkScoring

Enrichment:Funding (8 grants)Impact (FWCI 3.05)OA: hybridTopics (56)IDs (PubMed, PMC, OpenAlex)Annotations (1)SDGs (2)

FAIR Checklist

Context only (not used in score)

Findable (1/2)

Has DOI

Accessible (1/2)

Open Access

Interoperable (0/2)

Reusable (0/3)

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Authors (13)

Christopher A. Miller ORCID,Lauren Shea ORCID,Xuntian Jiang ORCID,Miguel A. Guzmán,Randy J. Chandler ORCID

Live enrichment

PubMed:33388420 PMC:PMC7854295 OpenAlex:https://openalex.org/W3114757933

National Human Genome Research Institute

Grant: 1ZIAHG200318-17

Investigations of Methylmalonic Acidemia and Related Disorders

National Institutes of Health

Grant: R01 NS100779

National Institutes of Health

Grant: R35 CA197561

NIDDK NIH HHS

Grant: P30 DK020579

Intramural NIH HHS

Grant: ZIA HG200318

National Institutes of Health

Grant: 5R01NS100779-05

Next Generation Treatment for Krabbe Disease

National Institutes of Health

Grant: 5R35CA197561-04

Molecular Pathogenesis of Acute Myeloid Leukemia

International Foundation for Research in Paraplegia

FWCI

3.05

Citation Percentile

0.9%

Citation Trend

2021

2022

2023

2024

2025

2026

hybridLicense: cc-by-nc-nd

journalhttp://www.cell.com/article/S1525001620307243/pdf

publisherhttp://www.cell.com/article/S1525001620307243/pdf

publisherhttps://api.elsevier.com/content/article/PII:S1525001620307243?httpAccept=text/xml

publisherhttps://api.elsevier.com/content/article/PII:S1525001620307243?httpAccept=text/plain

journalhttps://doi.org/10.1016/j.ymthe.2020.12.031

Fields of Study

Lysosomal Storage Disorders ResearchTrypanosoma species research and implicationsStudies on Chitinases and Chitosanases0301 basic medicine0303 health sciences03 medical and health sciencesAnimalsBone Marrow TransplantationCarcinoma, HepatocellularCombined Modality TherapyDependovirusDisease Models, AnimalGenetic TherapyGenetic VectorsLeukodystrophy, Globoid CellLiver NeoplasmsMice

MeSH Terms

DependovirusAnimalsCombined Modality TherapyDisease Models, AnimalGenetic VectorsCarcinoma, HepatocellularLeukodystrophy, Globoid CellLiver NeoplasmsGenetic TherapyBone Marrow TransplantationMice

Keywords

Krabbe diseaseToxicityMedicineTerm (time)DiseasePharmacologyInternal medicineLeukodystrophyGene therapyHepatocellular carcinomaAdeno-associated virusBone Marrow TransplantationCarcinoma, HepatocellularAnimalCarcinomaGenetic VectorsLiver Neoplasms610HepatocellularGenetic TherapyDependovirusGloboid CellCombined Modality TherapyLeukodystrophy, Globoid CellDisease Models, AnimalMiceDisease ModelsAnimals

Sustainable Development Goals

SDG 3: 3. Good healthSDG 0: Good health and well-being