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In utero genetic therapy: Treatment of early onset neurological disorders before they start

Molecular Therapy(2025)10.1016/j.ymthe.2025.06.012Source: DataRank Database

In utero genetic therapy: Treatment of early onset neurological disorders before they start is a research paper published in Molecular Therapy (2025). On theSindex it has a DataRank of 0. It has been cited 6 times.

N/A

0DataRank · unranked

Scored on demand from live citation data

Open Access6 citations

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›Methodology & internals

datarank_citation_only_1hop_v6· scope data_onlyMethodology

Pipeline:MetadataData-paper checkEnrichmentCitation networkScoring

Enrichment:Funding (4 grants)Impact (FWCI 4.54)OA: greenTopics (10)IDs (PubMed, PMC, OpenAlex)Annotations (1)SDGs (1)

FAIR Checklist

Context only (not used in score)

Findable (1/2)

Has DOI

Accessible (1/2)

Open Access

Interoperable (0/2)

Reusable (0/3)

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Authors (4)

Stephen M. Brown ORCID,Tippi C. MacKenzie ORCID,Charlotte J. Sumner ORCID,Beltran Borges ORCID

Live enrichment

PubMed:40570841 PMC:PMC12266014 OpenAlex:https://openalex.org/W4411633676

NINDS NIH HHS

Grant: R35 NS122306

Biogen Inc

National Institutes of Health

UCSF Center for Maternal-Fetal Precision Medicine

FWCI

4.54

Citation Percentile

1.0%

Citation Trend

2025

2026

greenLicense: http://creativecommons.org/licenses/by-nc-nd/4.0/

repositoryhttps://pmc.ncbi.nlm.nih.gov/articles/PMC12266014/

publisherhttps://api.elsevier.com/content/article/PII:S1525001625004630?httpAccept=text/xml

publisherhttps://api.elsevier.com/content/article/PII:S1525001625004630?httpAccept=text/plain

journalhttps://doi.org/10.1016/j.ymthe.2025.06.012

Fields of Study

Neurogenetic and Muscular Disorders ResearchCongenital heart defects researchWilliams Syndrome Research

Keywords

In uteroMedicinePediatricsBiologyGeneticsPregnancyFetus

Sustainable Development Goals

SDG 0: Good health and well-being

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In utero genetic therapy: Treatment of early onset neurological disorders before they start

FAIR Checklist

Authors (4)

Funding (4 grants)

Impact

Open Access

Topics

Annotations (Europe PMC)

Related Papers (10)