Pilot corpus: NIH-funded biomedical datasets. Any DOI can be scored on demand — network effects sharpen as coverage grows.

Development of an AAV-based gene therapy for the ocular phenotype of Friedreich’s ataxia

Molecular Therapy(2025)10.1016/j.ymthe.2025.10.048Source: DataRank Database

Development of an AAV-based gene therapy for the ocular phenotype of Friedreich’s ataxia is a research paper published in Molecular Therapy (2025). On theSindex it has a DataRank of 0. It has been cited 1 time.

N/A

0DataRank · unranked

Scored on demand from live citation data

Open Access1 citations

Download PDF

Cite:

Linked data & code

uniprot doi

DataRank reads this dataset's downstream impact straight off the citation graph — no black box, no proprietary weighting. How is this computed?

›Methodology & internals

datarank_citation_only_1hop_v6· scope data_onlyMethodology

Pipeline:MetadataData-paper checkEnrichmentCitation networkScoring

Enrichment:Funding (2 grants)Impact (FWCI 0.45)OA: greenTopics (46)IDs (PubMed, PMC, OpenAlex)Annotations (2)

FAIR Checklist

Context only (not used in score)

Findable (1/2)

Has DOI

Accessible (1/2)

Open Access

Interoperable (0/2)

Reusable (0/3)

FAIR checklist signals are shown for context only and do not affect DataRank scoring.

Run a calibrated FAIR evaluation for this paper →

We only score data papers we can read in full — never from an abstract alone.

Authors (15)

Siddhant Gupte ORCID,Emily Xu ORCID,Kaitlyn R. Calabro ORCID,Hannah Friend,Sean M. Crosson

Live enrichment

PubMed:41137390 PMC:PMC12882371 OpenAlex:https://openalex.org/W4415517924

National Institutes of Health

Grant: R01 EY024280

Friedreich's Ataxia Research Alliance

Grant: R01 EY031042

FWCI

0.45

Citation Percentile

0.6%

Citation Trend

2026

greenLicense: cc-by

repositoryhttps://mouseion.jax.org/stfb2026/34

publisherhttps://api.elsevier.com/content/article/PII:S152500162500869X?httpAccept=text/xml

publisherhttps://api.elsevier.com/content/article/PII:S152500162500869X?httpAccept=text/plain

journalhttps://doi.org/10.1016/j.ymthe.2025.10.048

Fields of Study

Genetic Neurodegenerative DiseasesMitochondrial Function and PathologyEndoplasmic Reticulum Stress and DiseaseFriedreich AtaxiaGenetic TherapyDependovirusAnimalsMiceGenetic VectorsFrataxinDisease Models, AnimalPhenotypeIron-Binding ProteinsMice, KnockoutHumansRetinal Ganglion CellsRetina

MeSH Terms

FrataxinDependovirusAnimalsDisease Models, AnimalFriedreich AtaxiaGenetic VectorsHumansPhenotypeRetinaRetinal Ganglion CellsGenetic TherapyMice, KnockoutIron-Binding ProteinsMice

Keywords

FrataxinRetinalAtaxiaGenetic enhancementPhenotypeRetinal degenerationLoss functionOptic nerveAdeno-associated virusRetinal ganglion cellAAVFriedreich's AtaxiaMouse ModelIntravitreal DeliveryOcular Gene Therapy

Development of an AAV-based gene therapy for the ocular phenotype of Friedreich’s ataxia

FAIR Checklist

Authors (15)

Funding (2 grants)

Impact

Open Access

Topics

Annotations (Europe PMC)