Donald B. Kohn

Also affiliated with University of California System, Los Angeles Medical Center, Broad Center

Biochemistry, Genetics and Molecular BiologyMedicineImmunology and Microbiology

Pilot corpus only

This score is computed over theSindex pilot corpus and does not cover the full scientific literature. Scores are relative to papers we have ingested — papers, authors, and institutions outside the pilot are not represented. Methodology.

Top 100%percentile

0Author DataRank

Indexed papers

0in pilot corpus

datarank_citation_only_1hop_v6· scope data_onlyMethodology

Papers

Driven by 53 papers. Top paper: “Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency”.

Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency

New England Journal of Medicine(2021)10.1056/nejmoa2027675

N/A

5.1DataRank · unranked

219 citations

Claire Booth, Kit L. Shaw, Jinhua Xu‐Bayford, Elizabeth Garabedian, Valentina Trevisan +48 more

Excellent outcomes following hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

Blood(2020)10.1182/blood.2019002939

N/A

4.1DataRank · unranked

138 citations

Aleksandra Petrović, Ruta Brazauskas, Xuerong Liu, Linda M. Griffith, Hans D. Ochs +47 more

Infections in Infants with SCID: Isolation, Infection Screening, and Prophylaxis in PIDTC Centers

Journal of Clinical Immunology(2020)10.1007/s10875-020-00865-9

N/A

2.1DataRank · unranked

58 citations

Nicola Wright, Natalia S. Chaimowitz, Blachy J. Dávila Saldaña, Holly Miller, Michael D. Keller +54 more

Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency

Blood(2021)10.1182/blood.2020010260

N/A

2.0DataRank · unranked

48 citations

Omar Habib, Kit L. Shaw, Elizabeth Garabedian, Denise A. Carbonaro-Sarracino, Dayna Terrazas +31 more

High-level correction of the sickle mutation is amplified in vivo during erythroid differentiation

iScience(2022)10.1016/j.isci.2022.104374

N/A

1.5DataRank · unranked

52 citations

Mark A. DeWitt, Stacia K. Wyman, Jonathan T. Vu, Seok‐Jin Heo, Shirley Shao +15 more

Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTC

Blood(2022)10.1182/blood.2022016196

N/A

1.5DataRank · unranked

51 citations

Brent R. Logan, Susan E. Prockop, Rebecca H. Buckley, Caroline Y. Kuo, Linda M. Griffith +45 more

Evidence generation and reproducibility in cell and gene therapy research: A call to action

Molecular Therapy - Methods & Clinical Development(2021)10.1016/j.omtm.2021.06.012

N/A

0.934DataRank · unranked

24 citations

Aris Angelis, Frederick R. Appelbaum, Nancy C. Andrews, Susan E. Bates, Arlene S. Bierman +33 more

Genotype, oxidase status, and preceding infection or autoinflammation do not affect allogeneic HCT outcomes for CGD

Blood(2023)10.1182/blood.2022019586

N/A

0.816DataRank · unranked

26 citations

Danielle E. Arnold, Suhag Parikh, Brent R. Logan, Rebecca Marsh, Linda M. Griffith +64 more

Intestinal microbiome and metabolome signatures in patients with chronic granulomatous disease

Journal of Allergy and Clinical Immunology(2023)10.1016/j.jaci.2023.07.022

N/A

0.757DataRank · unranked

26 citations

Yu Han, Christa S. Zerbe, Theo Heller, Suk See De Ravin, Samantha A. Kreuzberg +52 more

Hematopoietic Cell Transplantation in Patients With Primary Immune Regulatory Disorders (PIRD): A Primary Immune Deficiency Treatment Consortium (PIDTC) Survey

Frontiers in Immunology(2020)10.3389/fimmu.2020.00239

N/A

0.663DataRank · unranked

82 citations

Jennifer W. Leiding, Xuerong Liu, Brent R. Logan, Lauri M. Burroughs, Eric J. Allenspach +55 more

Evaluation of clonal hematopoiesis in pediatric ADA-SCID gene therapy participants

Blood Advances(2022)10.1182/bloodadvances.2022007803

N/A

0.491DataRank · unranked

7 citations

Thomas D. Lee, Traci L. Toy, Judith Carroll, Lilian R. Polsky, Beatriz Campo Fernandez +4 more

Previous Infection Combined with Vaccination Produces Neutralizing Antibodies with Potency against SARS-CoV-2 Variants

mBio(2021)10.1128/mbio.02656-21

N/A

0.434DataRank · unranked

17 citations

Christian Hofmann, Ayub Ali, Paul Ayoub, Donald B. Kohn, Otto O. Yang +1 more

Creating New β-Globin-Expressing Lentiviral Vectors by High-Resolution Mapping of Locus Control Region Enhancer Sequences

Molecular Therapy — Methods & Clinical Development(2020)10.1016/j.omtm.2020.04.006

N/A

0.434DataRank · unranked

17 citations

Feiyang Ma, Mildred J. Unti, Devin Brown, Paul G. Ayoub, Curtis Tam +10 more

Human cancer-targeted immunity via transgenic hematopoietic stem cell progeny

Nature Communications(2025)10.1038/s41467-025-60816-z

N/A

0.281DataRank · unranked

4 citations

Nataly Naser Al Deen, Cole W. Peters, Begoña Comı́n-Anduix, Egmidio Medina, Cristina Puig-Saus +28 more

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

Blood Advances(2025)10.1182/bloodadvances.2025017662

N/A

0.165DataRank · unranked

2 citations

Blachy J. Dávila Saldaña, Ruta Brazauskas, Sravya Gethika Dammalapati, Linda M. Griffith, Ami J. Shah +57 more

Umbilical Cord Blood Transplantation Provides an Alternative for Patients With Chronic Granulomatous Disease Lacking HLA-Matched Donors: A PIDTC Report

Transplantation and Cellular Therapy(2025)10.1016/j.jtct.2025.05.020

N/A

0.104DataRank · unranked

1 citations

Jennifer W. Leiding, Brent R. Logan, Rebecca Marsh, Linda M. Griffith, Eyal Grunebaum +36 more

Influence of donor age and comorbidities on transduced human adipose-derived stem cell in vitro osteogenic potential

Gene Therapy(2022)10.1038/s41434-022-00367-w

N/A

0DataRank · unranked

20 citations

Jennifer A. Bell, Matthew C. Gallo, Stephanie W. Chang, Sofia Bougioukli, Osamu Sugiyama +9 more

Replication competent retrovirus testing (RCR) in the National Gene Vector Biorepository: No evidence of RCR in 1,595 post-treatment peripheral blood samples obtained from 60 clinical trials

Molecular Therapy(2022)10.1016/j.ymthe.2022.12.006

N/A

0DataRank · unranked

11 citations

Jing Yao, Kimberley House, Lisa Duffy, Prasad S. Adusumilli, Rachel K. Beyer +26 more

Aberrant T-cell exhaustion in severe combined immunodeficiency survivors with poor T-cell reconstitution after transplantation

Journal of Allergy and Clinical Immunology(2022)10.1016/j.jaci.2022.08.004

N/A

0DataRank · unranked

7 citations

Inès Boufaied, Benoîte Bourdin, Saideep Gona, Haley E. Randolph, Brent R. Logan +28 more

Successes and challenges in clinical gene therapy

Gene Therapy(2023)10.1038/s41434-023-00390-5

N/A

0DataRank · unranked

164 citations

Yvonne Y. Chen, Melissa J. Spencer, Donald B. Kohn

Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium

The Lancet(2023)10.1016/s0140-6736(23)00731-6

N/A

0DataRank · unranked

121 citations

Brent R. Logan, Jennifer M. Puck, Elizabeth Dunn, Rebecca H. Buckley, Morton J. Cowan +60 more

Human T cell generation is restored in CD3δ severe combined immunodeficiency through adenine base editing

Cell(2023)10.1016/j.cell.2023.02.027

N/A

0DataRank · unranked

83 citations

Gloria Yiu, Patrick Chang, Gregory A. Newby, Beatriz Campo-Fernández, Sorel Fitz‐Gibbon +18 more

Secondary Neoplasms After Hematopoietic Cell Transplant for Sickle Cell Disease

Journal of Clinical Oncology(2023)10.1200/jco.22.01203

N/A

0DataRank · unranked

55 citations

Ruta Brazauskas, David A. Williams, Mark C. Walters, Andrew St. Martin, Benjamin L. Jacobs +20 more

Posttransplantation late complications increase over time for patients with SCID: A Primary Immune Deficiency Treatment Consortium (PIDTC) landmark study

Journal of Allergy and Clinical Immunology(2023)10.1016/j.jaci.2023.09.027

N/A

0DataRank · unranked

21 citations

Monica S. Thakar, Ami J. Shah, Brent R. Logan, Linda M. Griffith, Huaying Dong +53 more

Gene Therapy for β-Hemoglobinopathies: From Discovery to Clinical Trials

Viruses(2023)10.3390/v15030713

N/A

0DataRank · unranked

25 citations

Paul G. Ayoub, Kevyn L. Hart, Donald B. Kohn, Eva Segura

Fluorinated Silane-Modified Filtroporation Devices Enable Gene Knockout in Human Hematopoietic Stem and Progenitor Cells

ACS Applied Materials & Interfaces(2023)10.1021/acsami.3c07045

N/A

0DataRank · unranked

10 citations

Alexandra M. Mendoza, Tzu‐Ting Chiou, Philseok Kim, Joanna Aizenberg, Donald B. Kohn +4 more

263 A lipid nanoparticle arsenal to correct cystic fibrosis in airway stem cells

Journal of Cystic Fibrosis(2023)10.1016/s1569-1993(23)01191-8

N/A

0DataRank · unranked

0 citations

Paul G. Ayoub, Erika Duggan, J. Khorsandi, Diego Banuet, Abhishek Purkayastha +4 more

Antiviral cellular therapy for enhancing T-cell reconstitution before or after hematopoietic stem cell transplantation (ACES): a two-arm, open label phase II interventional trial of pediatric patients with risk factor assessment

Nature Communications(2024)10.1038/s41467-024-47057-2

N/A

0DataRank · unranked

26 citations

Patrick J. Hanley, Yueh‐Yun Chi, Paibel Aguayo‐Hiraldo, Christopher C. Dvorak, Michael R. Verneris +44 more

High symptom burden in female X-linked chronic granulomatous disease carriers

Clinical Immunology(2024)10.1016/j.clim.2024.110364

N/A

0DataRank · unranked

11 citations

Athanasios Tsalatsanis, Jessica Trotter, Danielle E. Arnold, Jacqueline D. Squire, Sharon A. Kidd +24 more

Allogeneic hematopoietic cell transplantation is effective for p47phox chronic granulomatous disease: A Primary Immune Deficiency Treatment Consortium study

Journal of Allergy and Clinical Immunology(2024)10.1016/j.jaci.2024.01.013

N/A

0DataRank · unranked

10 citations

Danielle E. Arnold, Brent R. Logan, Suhag Parikh, Rebecca Marsh, Linda M. Griffith +36 more

Relevance of lymphocyte proliferation to PHA in severe combined immunodeficiency (SCID) and T cell lymphopenia

Clinical Immunology(2024)10.1016/j.clim.2024.109942

N/A

0DataRank · unranked

8 citations

Amrita Basu, Jennifer Heimall, Elizabeth Dunn, Alison Yip, Malika Kapadia +52 more

A novel high-titer, bifunctional lentiviral vector for autologous hematopoietic stem cell gene therapy of sickle cell disease

Molecular Therapy — Methods & Clinical Development(2024)10.1016/j.omtm.2024.101254

N/A

0DataRank · unranked

5 citations

Boya Liu, Devin Brown, Beatriz Campo-Fernández, Kevin J. Tam, Katherine Orr +5 more

Quantifying the mutational landscape of retroviral and lentiviral vectors in gene therapy patients

Molecular Therapy(2025)10.1016/j.ymthe.2025.05.034

N/A

0DataRank · unranked

2 citations

Ralph Valentine Crisostomo, Annika Mittelhauser, Lingyu Zhan, Nika Kononov, Kathryn Bradford +2 more

Clinical spectrum of Wiskott-Aldrich syndrome carriers: Self-reported survey of 193 carriers

Clinical Immunology(2025)10.1016/j.clim.2025.110658

N/A

0DataRank · unranked

1 citations

Adrianna Westbrook, Linda M. Griffith, David Hagin, Sumathi Iyengar, Christina Mangurian +22 more

Lentiviral vectors for hematopoietic stem cell gene therapy restore α-globin expression in α-thalassemia red blood cells

Cell Reports Medicine(2025)10.1016/j.xcrm.2025.102362

N/A

0DataRank · unranked

1 citations

Kevyn L. Hart, Beatriz Campo Fernandez, Devin Brown, Kevin J. Tam, Andrea Gutierrez Garcia +14 more

Oligonucleotide synthesis errors are a source of untoward variation in HDR-mediated gene editing

bioRxiv (Cold Spring Harbor Laboratory)(2025)10.1101/2025.07.08.663753

N/A

0DataRank · unranked

1 citations

Zulema Romero, Seok‐Jin Heo, Marian Navarrete, Netravathi Krishnappa, Donald B. Kohn +4 more

Outcomes following matched sibling donor transplantation for severe combined immunodeficiency: a report from the PIDTC

Blood Advances(2025)10.1182/bloodadvances.2025016812

N/A

0DataRank · unranked

0 citations

Brent R. Logan, Xuerong Liu, Jasmeen Dara, Rebecca H. Buckley, Joseph H. Oved +48 more

Neurodevelopmental outcomes following hematopoietic cell transplantation for patients with severe combined immunodeficiency (SCID): A PIDTC study

Journal of Human Immunity(2025)10.70962/jhi.20250163

N/A

0DataRank · unranked

0 citations

Sharon A. Kidd, Brent R. Logan, Farheen Chunara, Jennifer Heimall, Linda M. Griffith +32 more

Lentiviral gene therapy for X-linked chronic granulomatous disease

Nature Medicine(2020)10.1038/s41591-019-0735-5

N/A

0DataRank · unranked

254 citations

Claire Booth, Elizabeth M. Kang, Sung‐Yun Pai, Kit L. Shaw, Giorgia Santilli +33 more

Artificial thymic organoids represent a reliable tool to study T-cell differentiation in patients with severe T-cell lymphopenia

Blood Advances(2020)10.1182/bloodadvances.2020001730

N/A

0DataRank · unranked

100 citations

Francesca Pala, Enrica Calzoni, Ottavia M. Delmonte, Kerry Dobbs, Cameron L. Gardner +20 more

Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy

Biology of Blood and Marrow Transplantation(2020)10.1016/j.bbmt.2020.07.004

N/A

0DataRank · unranked

10 citations

Siyu Liu, Maja Krajinović, Marc Ansari, Elizabeth Garabedian, John Tse +6 more

AT1R Activating Autoantibodies in Hematopoietic Stem Cell Transplantation

Biology of Blood and Marrow Transplantation(2020)10.1016/j.bbmt.2020.07.029

N/A

0DataRank · unranked

9 citations

Meghan Pearl, Donald B. Kohn, Patricia L. Weng, Ora Yadin, La Vette Bowles +3 more

Supramolecular nanosubstrate–mediated delivery system enables CRISPR-Cas9 knockin of hemoglobin beta gene for hemoglobinopathies

Science Advances(2020)10.1126/sciadv.abb7107

N/A

0DataRank · unranked

42 citations

Shih‐Jie Chou, Jindian Li, Wenqiao Hui, Wenfei Liu, Na Sun +20 more

Antiviral Drug Screen of Kinase inhibitors Identifies Cellular Signaling Pathways Critical for SARS-CoV-2 Replication

bioRxiv (Cold Spring Harbor Laboratory)(2020)10.1101/2020.06.24.150326

N/A

0DataRank · unranked

26 citations

Arun Sharma, Arunachalam Ramaiah, Chandani Sen, Donald B. Kohn, Brigitte N. Gomperts +4 more

Correction: Chronic Granulomatous Disease-Associated IBD Resolves and Does Not Adversely Impact Survival Following Allogeneic HCT

Journal of Clinical Immunology(2020)10.1007/s10875-020-00852-0

N/A

0DataRank · unranked

3 citations

Jennifer W. Leiding, Brent R. Logan, Linda M. Griffith, Danielle E. Arnold, Élie Haddad +50 more

Gene Therapy: Charting a Future Course—Summary of a National Institutes of Health Workshop, April 12, 2013

UNC Libraries(2020)10.17615/bazj-3394

N/A

0DataRank · unranked

0 citations

Howard J. Federoff, Luk H. Vandenberghe, Aravind Asokan, Mehrdad Abedi, Laurie Zoloth +27 more

Antiviral drug screen identifies DNA-damage response inhibitor as potent blocker of SARS-CoV-2 replication

Cell Reports(2021)10.1016/j.celrep.2021.108940

N/A

0DataRank · unranked

119 citations

Arun Sharma, Arunachalam Ramaiah, Chandani Sen, Arunima Purkayastha, Donald B. Kohn +23 more

Development of allogeneic HSC-engineered iNKT cells for off-the-shelf cancer immunotherapy

Cell Reports Medicine(2021)10.1016/j.xcrm.2021.100449

N/A

0DataRank · unranked

104 citations

Yang Zhou, Kwang Gi Kim, Yanni Zhu, Feiyang Ma, Jiaji Yu +24 more

Gene delivery using AAV8 in vivo for disease stabilization in a bimodal gene therapy approach for the treatment of ADA-deficient SCID

Molecular Therapy — Methods & Clinical Development(2021)10.1016/j.omtm.2021.02.007

N/A

0DataRank · unranked

2 citations

Krista Chun, Danielle N. Clark, Michael L. Kaufman, Xiangyang Jin, Xiaoyan Wang +2 more

The diagnosis of severe combined immunodeficiency (SCID): The Primary Immune Deficiency Treatment Consortium (PIDTC) 2022 Definitions

Journal of Allergy and Clinical Immunology(2022)10.1016/j.jaci.2022.10.022

N/A

0DataRank · unranked

127 citations

Élie Haddad, Jennifer Heimall, Elizabeth Dunn, Rebecca H. Buckley, Donald B. Kohn +14 more

The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions

Journal of Allergy and Clinical Immunology(2022)10.1016/j.jaci.2022.10.021

N/A

0DataRank · unranked

39 citations

Élie Haddad, Jennifer Heimall, Elizabeth Dunn, Morton J. Cowan, Sung‐Yun Pai +46 more

Meeting FDA Guidance recommendations for replication-competent virus and insertional oncogenesis testing

Molecular Therapy — Methods & Clinical Development(2022)10.1016/j.omtm.2022.11.009

N/A

0DataRank · unranked

33 citations

Tsai‐Yu Lin, Danilo Pellin, Donald B. Kohn, Kenneth Cornetta

Diverse Approaches to Gene Therapy of Sickle Cell Disease

Annual Review of Medicine(2022)10.1146/annurev-med-042921-021707

N/A

0DataRank · unranked

32 citations

Kevyn L. Hart, Donald B. Kohn, Shanna White